clinical trials

/Tag: clinical trials

Clinical trials: Your questions answered

Clinical trials: Your questions answered Promising new treatments for many muscle and nerve conditions have been developed in recent years, promising enough in fact, for pharmaceutical companies and other funding bodies to invest in expensive clinical trials. On average only about one fifth of treatments that go to clinical trial are proven to be safe [...]

By | 2018-07-02T15:14:44+00:00 July 2nd, 2018|disorders, research, trials|0 Comments

MDA’s $1,000,000 Making a Difference

MDA Support of “Muscle Clinic” at RCH exceeds $1,000,000 creating world’s first dedicated multi-disciplinary Clinic Sometimes we need a reminder to realise just how far Muscular Dystrophy Australia’s support of the MD Community extends. The relationship between the MDA and RCH goes back some 26 years, when MDA was funding a dedicated MD Social Worker [...]

By | 2018-06-01T03:49:05+00:00 September 13th, 2017|about, information, news, research, Support Services, trials|0 Comments

Looking Back and Moving Forward

Launch of National Duchenne Muscular Dystrophy Register On Monday November 15th 2010, the Director General of Health launched the Duchenne Muscular Dystrophy (DMD) Registry. Patient registries are infrastructure that supports clinical and translational research. The DMD registry was created in response to developments in genetic technology and in particular clinical trials currently being planned, that [...]

By | 2017-06-28T17:30:17+00:00 June 28th, 2017|disorders, information, news, research, trials|0 Comments

FDA Approves Drug for Treatment of DMD

Chantal Coles PhD NMDRC provides a Research Update... On September 19th last year the U.S Food and Drug Administration (FDA) approved the first drug for the treatment of Duchenne Muscular Dystrophy, called EXONDYS 51™. This drug, formally known as Eteplirsen, is a gene modifying agent that bypasses a stop codon of the dystrophin, forming a [...]

By | 2018-06-01T03:49:09+00:00 April 3rd, 2017|information, research, trials|0 Comments

Dr Jason White – Back in the Lab

Recently, Dr. Jason White, lead researcher at the National Muscular Dystrophy Research Centre (NDMRC) at the Murdoch Children’s Research Institute, returned from six months of research in Vancouver, Canada. The purpose of this trip was to learn new techniques for research into Muscular Dystrophy and ensure Australia is up-to-date with all research developments and breakthroughs [...]

By | 2017-03-29T15:42:12+00:00 March 29th, 2017|information, research|0 Comments

Spinal Muscular Atrophy (SMA) Research Update

Spinal Muscular Atrophy (SMA) Research update and treatment - AUSTRALIA A research update by Prof. Monique Ryan Director, Department of Neurology Group Leader, Murdoch Children's Research Institute,  Royal Children's Hospital There has been a lot of activity in the clinical trial space for SMA in the last two years. Two hospitals in Australia- the The [...]

By | 2018-06-01T03:49:11+00:00 November 17th, 2016|atrophies, research, trials|0 Comments

Muscle Clinic

Muscle Clinic A world-first initiative, the MDA Neuromuscular Clinic is funded by MDA (we have invested in excess of $1.5 million) is an initiative work alongside Neurologists and their team of specialist, all forming part of the medical team monitoring and caring for our clients. We work in conjunction with RCH team to provide the [...]

By | 2018-07-06T16:44:27+00:00 October 24th, 2016|Comments Off on Muscle Clinic

Respiratory Care in MD

Respiratory care and ventilation There are many different neuromuscular conditions in which weakness of the breathing muscles requires monitoring and treatment and may eventually need some form of mechanical ventilation.  In Duchenne muscular dystrophy most boys/young men will need to start using a ventilator in their late teens to early twenties. In some other conditions [...]

By | 2018-06-01T03:47:58+00:00 July 23rd, 2016|Comments Off on Respiratory Care in MD