trials

Muscular Dystrophy Australia is your One-Stop-Shop

Dr Chantal Coles, Boris M Struk, Prof Kathryn North AC, and Chris Kintakis Muscular Dystrophy Australia is your one-stop-shop for expert information, support, research and trials. MDA works tirelessly to support clinical trials and expand clinical trial capacity for Australia. We have been on the Steering Committee of the National Registries for more than a [...]

By |2019-04-05T15:09:59+00:00April 5th, 2019|ambassador, Boris M Struk, news, research, trials|0 Comments

MDA – Hope in Research

MDA - Hope in Research MDA’s core mission is to provide support and hope to the MD community. We fund numerous research projects and trials in the hope that the quality of life of people with MD will improve and that eventually a cure will be found. #musculardystrophyaustralia #duchenne #duchenneawareness #clinicaltrials #raredisease #hope #cure4MD #research [...]

By |2019-04-15T12:13:45+00:00February 25th, 2019|information, research, trials|0 Comments

FSHD Research Projects

Advertising and promoting Facioscapulohumeral dystrophy (FSHD) Research Projects Researchers at The Royal Children’s Hospital are looking for children and adolescents aged 6-18 years who have been diagnosed with FSHD, to participate in one or both of these studies: The effect of the nutritional supplement (creatine monohydrate) on strength and muscle mass in children with FSHD [...]

By |2018-09-14T09:40:25+00:00September 14th, 2018|disorders, research, trials|0 Comments

DMD Lifetime Mobility Scale Research Study

DMD Lifetime Mobility Scale Research Study Muscular Dystrophy Australia is assisting the UC Davis Neuromuscular Research Center in USA to seek participants for an online survey about movement and daily living abilities for people with Duchenne muscular dystrophy. The Duchenne Muscular Dystrophy Life-Time Mobility Scale (DMD-LMS) is a set of questions that ask about how [...]

By |2018-08-16T18:28:09+00:00August 16th, 2018|disorders, research, trials|0 Comments

Clinical trials: Your questions answered

Clinical trials: Your questions answered Promising new treatments for many muscle and nerve conditions have been developed in recent years, promising enough in fact, for pharmaceutical companies and other funding bodies to invest in expensive clinical trials. On average only about one fifth of treatments that go to clinical trial are proven to be safe [...]

By |2018-12-22T14:24:52+00:00July 2nd, 2018|0 Comments

FDA Approves Drug for Treatment of DMD

Chantal Coles PhD NMDRC provides a Research Update... On September 19th last year the U.S Food and Drug Administration (FDA) approved the first drug for the treatment of Duchenne Muscular Dystrophy, called EXONDYS 51™. This drug, formally known as Eteplirsen, is a gene modifying agent that bypasses a stop codon of the dystrophin, forming a [...]

By |2018-06-01T03:49:09+00:00April 3rd, 2017|information, research, trials|0 Comments

Dr Jason White – Back in the Lab

Recently, Dr. Jason White, lead researcher at the National Muscular Dystrophy Research Centre (NDMRC) at the Murdoch Children’s Research Institute, returned from six months of research in Vancouver, Canada. The purpose of this trip was to learn new techniques for research into Muscular Dystrophy and ensure Australia is up-to-date with all research developments and breakthroughs [...]

By |2017-03-29T15:42:12+00:00March 29th, 2017|information, research|0 Comments

Spinal Muscular Atrophy (SMA) Research Update

Spinal Muscular Atrophy (SMA) Research update and treatment - AUSTRALIA A research update by Prof. Monique Ryan Director, Department of Neurology Group Leader, Murdoch Children's Research Institute,  Royal Children's Hospital There has been a lot of activity in the clinical trial space for SMA in the last two years. Two hospitals in Australia- the The [...]

By |2018-06-01T03:49:11+00:00November 17th, 2016|atrophies, research, trials|0 Comments