/Tag: trials

Clinical trials: Your questions answered

Clinical trials: Your questions answered Promising new treatments for many muscle and nerve conditions have been developed in recent years, promising enough in fact, for pharmaceutical companies and other funding bodies to invest in expensive clinical trials. On average only about one fifth of treatments that go to clinical trial are proven to be safe [...]

By | 2018-07-02T15:14:44+00:00 July 2nd, 2018|disorders, research, trials|0 Comments

FDA Approves Drug for Treatment of DMD

Chantal Coles PhD NMDRC provides a Research Update... On September 19th last year the U.S Food and Drug Administration (FDA) approved the first drug for the treatment of Duchenne Muscular Dystrophy, called EXONDYS 51™. This drug, formally known as Eteplirsen, is a gene modifying agent that bypasses a stop codon of the dystrophin, forming a [...]

By | 2018-06-01T03:49:09+00:00 April 3rd, 2017|information, research, trials|0 Comments

Dr Jason White – Back in the Lab

Recently, Dr. Jason White, lead researcher at the National Muscular Dystrophy Research Centre (NDMRC) at the Murdoch Children’s Research Institute, returned from six months of research in Vancouver, Canada. The purpose of this trip was to learn new techniques for research into Muscular Dystrophy and ensure Australia is up-to-date with all research developments and breakthroughs [...]

By | 2017-03-29T15:42:12+00:00 March 29th, 2017|information, research|0 Comments

Spinal Muscular Atrophy (SMA) Research Update

Spinal Muscular Atrophy (SMA) Research update and treatment - AUSTRALIA A research update by Prof. Monique Ryan Director, Department of Neurology Group Leader, Murdoch Children's Research Institute,  Royal Children's Hospital There has been a lot of activity in the clinical trial space for SMA in the last two years. Two hospitals in Australia- the The [...]

By | 2018-06-01T03:49:11+00:00 November 17th, 2016|atrophies, research, trials|0 Comments

Muscle Clinic

Muscle Clinic A world-first initiative, the MDA Neuromuscular Clinic is funded by MDA (we have invested in excess of $1.5 million) is an initiative work alongside Neurologists and their team of specialist, all forming part of the medical team monitoring and caring for our clients. We work in conjunction with RCH team to provide the [...]

By | 2018-07-06T16:44:27+00:00 October 24th, 2016|Comments Off on Muscle Clinic

Diabetes Research…

Diabetes Research... may help autoimmune muscle diseases Exciting new research may lead to the development of treatments for autoimmune disease which is good news for the approximately 6000 Australians affected by the muscle diseases myasthenia gravis, Guillain-Barre Syndrome and chronic inflammatory demyelinating polyneuropathy (CIDP). Diabetes researchers in San Francisco identified a distinctive type of immune [...]

By | 2018-07-02T14:46:21+00:00 July 23rd, 2016|Comments Off on Diabetes Research…

Burnt sugar treatment for MD?

Burnt sugar treatment for MD? Burnt sugar treatment for muscular dystrophy? You may have seen headlines on the internet about researchers testing a substance found in burnt sugar, beer, cola and some lollies as a treatment for muscular dystrophy. Sounds like a joke doesn’t it? But actually this early stage research is based on the [...]

By | 2018-07-02T14:38:35+00:00 July 23rd, 2016|Comments Off on Burnt sugar treatment for MD?

Duchenne MD research news update 2015

Duchenne MD research news update 2015 There have been several developments in the past month with regard to the development of treatments for Duchenne MD. This includes two “firsts” for Duchenne MD – the first successful phase 3 clinical trial and the first New Drug Application to the US regulatory authorities (the FDA). In addition, [...]

By | 2018-07-02T14:49:23+00:00 July 23rd, 2016|Comments Off on Duchenne MD research news update 2015